We report on gene therapy for Wiskott-Aldrich syndrome, a breakthrough treatment showing promising results in clinical trials (NCT03537496), with 90% efficacy rates, now available at top US hospitals.
Scientists Turn Off Disease Genes: RNA Interference Technology That Silences Genetic Disorders
Discover the power of gene silencing RNA interference in treating genetic disorders. Learn about its applications, benefits, and latest research findings in our ultimate guide.